HealthQuill Genetic Disorder
Britain’s National Health Service will provide a gene therapy that may cure sickle cell disease for patients 12 years and older, according to a National Institute for Health and Care Excellence (NICE) statement.
Drugs Health Medical

UK’s NHS to provide gene therapy that may cure sickle cell  disease in adults

Britain’s National Health Service will provide a gene therapy that may cure sickle cell disease for patients 12 years and older, according to.

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IntraBio Inc, a biotechnology company focused on rare and neurodegenerative diseases, got the US regulator’s nod for a drug to treat a certain type of Niemann-Pick disease in adults and pediatric patients weighing about 15 kilograms.
Drugs Health Pharma

IntraBio Inc.’s drug for neurogenerative disorder gets US regulator’s nod

IntraBio Inc, a biotechnology company focused on rare and neurogenerative diseases, got the US regulator’s nod for a drug to treat a certain.

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The Food and Drug Administration has cleared X4 Pharmaceutical’s drug to treat a rare genetic disease that occurs in one in five million births.
Drugs Health Pharma

X4 Pharmaceutical’s drug to fight WHIM syndrome gets green light

HQ Team April 30, 2024: The Food and Drug Administration has cleared X4 Pharmaceutical’s drug to treat a rare genetic disease that occurs.

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