Gene therapy restores hearing in children with inherited deafness
Bharti Jayshankar January 25, 2024: A new gene therapy has demonstrated remarkable success in treating inherited deafness. Two separate studies, one conducted by.
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Novartis to pay $100m upfront to Voyager for gene therapies
HQ Team January 3, 2023: Voyager Therapeutics, Inc., will receive an upfront payment of $100 million from Switzerland-based Novartis AG to develop gene.
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Opinion: Sickle Cell Disease and gene therapy
By K. Leelamoni December 19, 2023: Recent reports about the FDA’s approval of gene therapy to treat Sickle Cell Anemia mark a major.
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Gene to treat chronic muscle disorders found
HQ team November 13, 2023: Researchers at the University of California, Irvine, have identified a gene that helps in muscle repair during regeneration..
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Alexion, Pfizer sign $1 billion accord for genomic medicines
HQ Team July 29, 2023: Alexion, AstraZeneca Rare Disease, an arm of AstraZeneca group, has signed a $1 billion pact with Pfizer for.
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Gene variant discovery may trigger new treatments for multiple sclerosis
HQ Team July 5, 2023: Researchers found a genetic variant that increases the severity of multiple sclerosis (MS) and may pave the way.
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FDA, EMA accept Pfizer’s BLP application for hemophilia therapy
HQ Team June 26, 2023: Pfizer Inc. announced that USFDA has accepted its biologics license application for treating bleeding disorders in adults through.
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FDA approves gene therapy for treatment of high-risk bladder cancer
The FDA approved Adstiladrin (nadofaragene firadenovec-vncg), a non-replicating adenoviral vector-based gene therapy for the treatment of high-risk bladder cancer.
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US scientists use zebrafish to fine-tune gene therapy
Scientists in the US used a mechanism that zebrafish rely on to repair their damaged hearts and then combined it with viral vectors.