Drugs Health Pharma

Deaf 18-month girl gets back hearing ability after gene therapy

HQ Team May 15, 2024: An 18-month-old baby girl, Opal Sandy, who was born deaf got back her hearing ability after gene therapy.

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Drugs Health Medical

Gene therapy restores hearing in children with inherited deafness

Bharti Jayshankar January 25, 2024: A new gene therapy has demonstrated remarkable success in treating inherited deafness. Two separate studies, one conducted by.

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Drugs Health Pharma

Novartis to pay $100m upfront to Voyager for gene therapies

HQ Team January 3, 2023: Voyager Therapeutics, Inc., will receive an upfront payment of $100 million from Switzerland-based Novartis AG to develop gene.

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Drugs Health Medical

Opinion: Sickle Cell Disease and gene therapy

By K. Leelamoni December 19, 2023: Recent reports about the FDA’s approval of gene therapy to treat Sickle Cell Anemia mark a major.

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Health Medical Pharma

Gene to treat chronic muscle disorders found

HQ team November 13, 2023: Researchers at the University of California, Irvine, have identified a gene that helps in muscle repair during regeneration..

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Drugs Health Medical Pharma

Gene therapy cure for sickle cell awaits advisory approval

HQ Team October 28, 2023: Advisers to the Food and Drug Administration (FDA) are set to review a gene therapy for sickle cell.

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Drugs Health Pharma

Alexion, Pfizer sign $1 billion accord for genomic medicines

HQ Team July 29, 2023: Alexion, AstraZeneca Rare Disease, an arm of AstraZeneca group, has signed a $1 billion pact with Pfizer for.

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Drugs Health Pharma

Gene variant discovery may trigger new treatments for multiple sclerosis

HQ Team July 5, 2023: Researchers found a genetic variant that increases the severity of multiple sclerosis (MS) and may pave the way.

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Drugs Medical Pharma

FDA, EMA accept Pfizer’s BLP application for hemophilia therapy

HQ Team June 26, 2023: Pfizer Inc. announced that USFDA has accepted its biologics license application for treating bleeding disorders in adults through.

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Drugs Medical

FDA approves gene therapy for treatment of high-risk bladder cancer

The FDA approved Adstiladrin (nadofaragene firadenovec-vncg), a non-replicating adenoviral vector-based gene therapy for the treatment of high-risk bladder cancer.

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